Ultragenyx

www.ultragenyx.com

1 Job

1,596 Employees

About the Company

Leading with purpose. Every day.

“Ultragenyx was founded to advance innovative medicines for rare and ultrarare diseases that have never been treated before. We are delivering transformative therapies across multiple indications, and we have one of the most robust and diverse clinical pipelines in rare disease. Our focus is on doing the right things for patients both during development and commercialization to deliver on the promise of these therapies in a way that's meaningful for rare disease communities.”

Emil D. Kakkis, M.D., Ph.D.
Chief Executive Officer and President

We have an inclusive culture of value and respect.

Ultragenyx brings novel products to those living with rare and ultrarare diseases with a focus on debilitating genetic diseases. Founded in 2010, we have rapidly built a diverse portfolio of approved therapies and products aimed at diseases with a high unmet medical need for which many have no approved therapies. It takes courage, care, talent, and dedication to make a meaningful impact for those living with rare diseases, their families and the rare disease community.

We put our people first, so they can take care of the rare disease community.

We purposefully cultivate and nurture a dynamic, supportive work environment where we encourage every team member to share their new ideas and help us unlock more possibilities. Our team is made up of exceptional and diverse people with a strong passion and commitment to helping those living with rare diseases. By embracing generosity, curiosity, inclusion, and humility we are constantly learning together—fostering an environment that supports profound growth and fulfillment.

If you want to have a meaningful impact, do the best work of your career while having fun and growing professionally and personally, come join our team!

Visit our community guidelines at: https://ultragenyx.co/community

Listed Jobs

Company Name: Ultragenyx
Job Title: Intern, Endpoint Development and Strategy
Job Description: Job title: Intern, Endpoint Development and Strategy Role Summary: Undergraduate internship focused on clinical outcomes assessment (COA) and qualitative research to characterize the impact of rare diseases and evaluate therapeutic interventions. The role includes literature analysis, interview transcription review, observational data interpretation, and preparation of scientific abstracts, poster presentations, and manuscript drafts for internal and external dissemination. Expactations: - Work full‑time remotely (35 hrs / week) with occasional travel to company offices. - Deliver literature reviews, data analyses, and written scientific outputs within project timelines. - Maintain clear, regular communication with supervisory staff regarding progress and deliverables. Key Responsibilities: - Conduct systematic literature reviews on diagnostic journeys, clinical presentation, assessment, and management of pediatric rare diseases. - Review and synthesize caregiver interview transcripts to capture disease‑impact insights. - Analyze cross‑sectional, observational patient cohort data and extract key findings. - Draft scientific abstracts and poster content aligned with conference and journal standards. - Compose a preliminary manuscript for submission to a rare disease or pediatric journal. - Organize and manage project documentation, ensuring accuracy and completeness. Required Skills: - Proficiency in literature search (PubMed, Web of Science, etc.). - Ability to conduct qualitative analysis and extract themes. - Data interpretation skills for cross‑sectional observational data. - Advanced Microsoft Office Suite (Word, Excel, PowerPoint) competency. - Strong organizational abilities and meticulous attention to detail. - Excellent written and verbal communication skills, capable of conveying complex scientific information clearly. Required Education & Certifications: - Current enrollment in a Bachelor’s (or equivalent MS/PharmD) program in a scientific or medical discipline, with at least one year of completed coursework. - Full‑time student status with plans to resume studies in the fall term.